Avalotcagene ontaparvovec
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Avalotcagene ontaparvovec (DTX301) is "a non-replicating, recombinant self-complimentary adeno-associated virus vector serotype 8 (scAAV8)-encoding human ornithine transcarbamylase". It is developed by Dimension Therapeutics for ornithine transcarbamylase (OTC) deficiency.[1][2][3]